Clinical trial for Sanfilippo syndrome

We are raising funds to help the quality of life of our "older" children who will never see a cure. We have a few studies/trials going on now, and are slated to open two new tclinical trials very soon.

$13,878 raised

$500,000 goal

/ 150


Giving quality of life to our dying children!

  1. Two clinical trials are in the works with Team Sanfilippo that are 100% funded by families. Please join us in giving children a fighting chance!
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